NIDO-361, a treatment for spinal and bulbar muscular atrophy (SBMA) now in a Phase 2 trial, was granted orphan drug ...
Disease progression in SMA types 2 and 3 is variable and influenced by functional status and age, according to a natural ...
Scientists conducted a cross-sectional study on the endocrine manifestations of 29 adults with SMA types 2, 3, or 4, at a ...
A move to a new home is not without challenges, but installing a vertical platform lift solves a big one, columnist Ari ...
“Alyssa, this is the best you’ve ever looked to me,” my gastroenterologist recently exclaimed during a routine appointment. Though I hadn’t felt my best internally, I took her word for it. After all, ...
Muscular Dystrophy Association (MDA) is the #1 voluntary health organization in the United States for people living with muscular dystrophy, ALS, and over 300 related neuromuscular conditions. For ...
Kevin Schaefer, who lives with SMA type 2, and neurologist Edward Smith, MD, reflect on their preferences for how to go about discussing difficult care decisions or bad news. Dr. Smith: I don’t think ...