US FDA expands approval for Alnylam's drug to treat rare heart disease
U.S. Food and Drug Administration approved Alnylam's drug to treat a rare and deadly heart disease on Thursday, allowing the ...
Mother with rare ALS touts 'miracle drug' that has stopped her disease
Raziel Green, 52, an active runner and mother of two, was diagnosed with a rare form of ALS in 2017. Since starting a ...
Country music icon retiring with rare disease. Here’s what to know
He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two ...
Woman with a rare disease that causes vertigo switches to Tesla car, says, she felt ‘peace and security’; Elon Musk reacts
A woman with a rare inner ear condition finds peace and security driving a Tesla Model 3 with Full Self-Driving, prompting a ...
An ‘Impossible’ Disease Outbreak in the Alps
In one tiny town, more than a dozen people were diagnosed with the rare neurodegenerative disease ALS. Why? I n March 2009, ...
BioSpace2d
Novartis’ Fabhalta Approved as First Therapy for Rare Kidney Disease
This is the third indication for Fabhalta after Novartis won FDA approval of the small molecule in paroxysmal nocturnal ...
Polar plunge raises thousands for John Hudson Dilgen, Staten Islander with rare skin disease
Dilgen, a 22-year-old Tottenville resident, has been battling epidermolysis bullosa (EB), a rare, life-threatening genetic ...
TechBullion3d
Biotech Community Curetopia Raises $1.77M to Advance Rare Disease Cures with Blockchain
Curetopia, a Biotech DAO, leverages decentralized science to accelerate rare disease research Zug, Switzerland, 20th March ...
Meet Daniela, the 12-year-old girl battling a rare disease who’s become the UConn women’s secret weapon
When the UConn women’s basketball team takes the court, they know that no matter what happens, they’ve got the support of one ...
Segway recalls 220,000 of its scooters due to a fall hazard that has resulted in 20 injuries
Segway is recalling about 220,000 of its scooters sold across the U.S. due to a fall hazard that has resulted in user ...
SHINE5d
Shanghai exhibition welcomes artwork from rare disease patients, including expats
At an event announcing the launch of the exhibition, Zhai Jin, a patient with osteogenesis imperfecta, a genetic bone ...