He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two ...

In one tiny town, more than a dozen people were diagnosed with the rare neurodegenerative disease ALS. Why? I n March 2009, ...

The Delhi High Court has observed that availability of a drug for treatment of rare diseases at economical and competitive ...

Raziel Green, 52, an active runner and mother of two, was diagnosed with a rare form of ALS in 2017. Since starting a ...

One of the most serious complications is the build-up of fluid in the lungs, significantly hindering breathing. Without ...

Jonathan James, CEO, Hope Charities, discusses the critical importance of maintaining access to life-saving medications for ...

U.S. Food and Drug Administration approved Alnylam's drug to treat a rare and deadly heart disease on Thursday, allowing the ...

In a groundbreaking achievement, Curetopia, the first Biotech Decentralized Autonomous Organization (DAO) built natively on ...

New cases suggests that other types of ticks, like the black-legged tick and the western black-legged tick, may also cause the condition.

The high court decision potentially opens the door for access to a generic version of the patented drug - Risdiplam - at a ...

This is the third indication for Fabhalta after Novartis won FDA approval of the small molecule in paroxysmal nocturnal ...