FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

NASA astronauts Sunita Williams, and Barry 'Butch' Wilmore returned to Earth after spending over 9 months in microgravity.

Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

The study involved 44 people with mild cognitive impairment. After six months, the volunteers who practiced strength training ...

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

A rare genetic condition, Spinal Muscular Atrophy (SMA) affects one in 7,000 people in India. It mostly affects children and ...